Toward An Effective Treatment For Spinal Muscular Atrophy

Courtesy ScienceDaily  Mon, 10/13/2008 - 21:30

Scientists are reporting a key advance toward developing the first effective drug treatment for spinal muscular atrophy (SMA), a genetic disease that involves motor neuron loss and occurs in 1 out of every 6,000 births.

SMA is the leading cause of hereditary infant death in the United States.


 

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