congenital amaurosis

No significant adverse effects were reported during a safety trial testing gene therapy on three patients with a type of hereditary blindness called Leber congenital amaurosis type 2.

In addition, the subjects said the vision in their treated eyes was slightly improved in dim lighting conditions.

Researchers have used gene therapy to safely restore vision in three young adults with a rare form of congenital blindness -- Leber congenital amaurosis.

Although the patients have not achieved normal eyesight, the preliminary results set the stage for further studies of an innovative treatment for this and possibly other retinal diseases.